Orphan drugs and orphan diseases: clin. realities and public policy ; proceedings of a conference held in Ann Arbor, Mich., Sept. 27 - 29, 1982
Gespeichert in:
| Format: | Buch |
|---|---|
| Sprache: | English |
| Veröffentlicht: |
New York
Liss
1983
|
| Schriftenreihe: | Progress in clinical and biological research
127 |
| Schlagworte: | |
| Online-Zugang: | Inhaltsverzeichnis |
| Beschreibung: | XXIX, 263 S. |
| ISBN: | 0845101277 |
Internformat
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Datensatz im Suchindex
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| adam_text | 612 O ORPHAN DRUGS AND ORPHAN DISEASES CLINICAL REALITIES AND PUBLIC
POLICY PROCEEDINGS OF A CONFERENCE HELD IN ANN ARBOR, MICHIGAN SEPTEMBER
27-29, 1982 EDITOR GEORGE J. BREWER DEPARTMENT OF HUMAN GENETICS AND
DEPARTMENT OF INTERNAL MEDICINE UNIVERSITY OF MICHIGAN MEDICAL SCHOOL
ANN ARBOR, MICHIGAN UNIVERSITATS- BIBLIOTHEK ALAN R. LISS, INC. * NEW
YORK^ CONTENTS CONTRIBUTORS IX PARTICIPANTS AND REGISTRANTS XI
DEDICATION XXI ACKNOWLEDGMENTS XXVI PREFACE GEORGE J. BREWER XXVII
PROGRESS AND PROBLEMS WITH ORPHAN DRUGS AND MANAGEMENT APPROACHES TO
ORPHAN DISEASES SESSION I THE ORPHAN DRUG PROBLEM IN
RADIOPHARMACEUTICAL RESEARCH AND DEVELOPMENT DENNIS P. SWANSON, THOMAS
MANGNER, AND WILLIAM H. BEIERWALTES 3 PERSISTENT PULMONARY HYPERTENSION
AND PROSTAGLANDIN D 2 JOSEPH B. PHILIPS AND RAYMOND K. LYRENE 21
THALASSEMIA ELMER B. BROWN 33 MYOCLONUS AND L-5-HYDROXYTRYPTOPHAN
(L-5HTP) MELVIN H. VAN WOERT 43 DISCUSSION 50 ANTIEPILEPTIC DRUG
DEVELOPMENT PROGRAM ROGER J. PORTER 53 DISCUSSION 63 SESSION II SODIUM
BENZOATE AND ARGININE: ALTERNATIVE PATHWAY THERAPY IN INBORN ERRORS OF
UREA SYNTHESIS MARK L. BATSHAW . . . 69 DISCUSSION 81 THE SPARSE FUR
MOUSE: AN ANIMAL MODEL FOR A HUMAN INBORN ERROR OF METABOLISM OF THE
UREA CYCLE ELAINE B. SPECTOR AND R.A. MAZZOCCHI 85 THE TREATMENT OF
SICKLE CELL ANEMIA AND WILSON S DISEASE WITH ZINC GEORGE J. BREWER AND
GRETCHEN M. HILL 97 DISCUSSION 111 EVALUATION OF SPECIFIC THERAPIES FOR
CYSTINOSIS JERRY A. SCHNEIDER 115 CYSTEAMINE TREATMENT OF NEPHROPATHIC
CYSTINOSIS JESS G: THOENE 125 DISCUSSION 129 VII VIII / CONTENTS KEYNOTE
ADDRESS WHO SHOULD DO WHAT? EDWARD N. BRANDT, JR 133 DISCUSSION 142
MAJOR ISSUES PANEL: THE ORPHAN DRUG PROBLEMS AND POSSIBLE SOLUTIONS
ORPHAN DRUGS AND ORPHAN DISEASES: THE CONSUMER S VIEWPOINT ABBEY S.
MEYERS 147 DISCUSSION 157 ORPHAN PRODUCTS: DEFINITION AND ACTIVITIES
MARION J. FINKEL 159 DISCUSSION 166 ORPHAN PRODUCTS ACTIVITIES OF THE
NATIONAL INSTITUTES OF HEALTH SAUL A. SCHEPARTZ 173 DISCUSSION 183
SCIENTISTS VIEWPOINTS ON ORPHAN DRUG PROBLEMS AND POSSIBLE SOLUTIONS
MELVIN H. VAN WOERT 187 DISCUSSION 194 ORPHAN DRUGS * A PHARMACEUTICAL
INDUSTRY VIEWPOINT GEORGE S. GOLDSTEIN 197 DISCUSSION 204 THE ORPHAN
DRUG ACT T. IRENE SANDERS 207 DISCUSSION 211 GENERAL DISCUSSION
FOLLOWING MAJOR ISSUES PANEL 217 POSTER SESSION PARTICIPANTS 231
CONSENSUS-SEEKING ROUND TABLES SUMMARY OF ROUND TABLE I: PROBLEMS WITH
ORPHAN DRUG DEVELOPMENT FROM THE PERSPECTIVE OF UNIVERSITY INVESTIGATORS
...... 235 SUMMARY OF ROUND TABLE II: THE ORPHAN DRUG PROBLEM FROM THE
PERSPECTIVE OF THE CONSUMER 239 SUMMARY OF ROUND TABLE III:
COMPUTER-ASSISTED DATA BASES 243 EDITOR S CLOSING COMMENTS 249
POSTSCRIPT 253 INDEX 255
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| physical | XXIX, 263 S. |
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| series2 | Progress in clinical and biological research |
| spelling | Orphan drugs and orphan diseases clin. realities and public policy ; proceedings of a conference held in Ann Arbor, Mich., Sept. 27 - 29, 1982 ed. George J. Brewer New York Liss 1983 XXIX, 263 S. txt rdacontent n rdamedia nc rdacarrier Progress in clinical and biological research 127 Seltene Krankheit (DE-588)4180919-1 gnd rswk-swf Chemotherapie (DE-588)4127083-6 gnd rswk-swf (DE-588)1071861417 Konferenzschrift 27.09.1982-29.09.1982 Ann Arbor, Mich. gnd-content Chemotherapie (DE-588)4127083-6 s Seltene Krankheit (DE-588)4180919-1 s DE-604 Brewer, George J. 1930- Sonstige (DE-588)128099607 oth Progress in clinical and biological research 127 (DE-604)BV000001177 127 GBV Datenaustausch application/pdf http://bvbr.bib-bvb.de:8991/F?func=service&doc_library=BVB01&local_base=BVB01&doc_number=000073400&sequence=000001&line_number=0001&func_code=DB_RECORDS&service_type=MEDIA Inhaltsverzeichnis |
| spellingShingle | Orphan drugs and orphan diseases clin. realities and public policy ; proceedings of a conference held in Ann Arbor, Mich., Sept. 27 - 29, 1982 Progress in clinical and biological research Seltene Krankheit (DE-588)4180919-1 gnd Chemotherapie (DE-588)4127083-6 gnd |
| subject_GND | (DE-588)4180919-1 (DE-588)4127083-6 (DE-588)1071861417 |
| title | Orphan drugs and orphan diseases clin. realities and public policy ; proceedings of a conference held in Ann Arbor, Mich., Sept. 27 - 29, 1982 |
| title_auth | Orphan drugs and orphan diseases clin. realities and public policy ; proceedings of a conference held in Ann Arbor, Mich., Sept. 27 - 29, 1982 |
| title_exact_search | Orphan drugs and orphan diseases clin. realities and public policy ; proceedings of a conference held in Ann Arbor, Mich., Sept. 27 - 29, 1982 |
| title_full | Orphan drugs and orphan diseases clin. realities and public policy ; proceedings of a conference held in Ann Arbor, Mich., Sept. 27 - 29, 1982 ed. George J. Brewer |
| title_fullStr | Orphan drugs and orphan diseases clin. realities and public policy ; proceedings of a conference held in Ann Arbor, Mich., Sept. 27 - 29, 1982 ed. George J. Brewer |
| title_full_unstemmed | Orphan drugs and orphan diseases clin. realities and public policy ; proceedings of a conference held in Ann Arbor, Mich., Sept. 27 - 29, 1982 ed. George J. Brewer |
| title_short | Orphan drugs and orphan diseases |
| title_sort | orphan drugs and orphan diseases clin realities and public policy proceedings of a conference held in ann arbor mich sept 27 29 1982 |
| title_sub | clin. realities and public policy ; proceedings of a conference held in Ann Arbor, Mich., Sept. 27 - 29, 1982 |
| topic | Seltene Krankheit (DE-588)4180919-1 gnd Chemotherapie (DE-588)4127083-6 gnd |
| topic_facet | Seltene Krankheit Chemotherapie Konferenzschrift 27.09.1982-29.09.1982 Ann Arbor, Mich. |
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