Exploring novel clinical trial designs for gene-based therapies: proceedings of a workshop
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| Main Author: | |
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| Format: | Electronic eBook |
| Language: | English |
| Published: |
Washington, D.C.
National Academies Press
[2020]
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| Subjects: | |
| Online Access: | TUM01 Volltext |
| Item Description: | Includes bibliographical references Intro -- FrontMatter -- Reviewers -- Acknowledgments -- Contents -- Boxes, Figures, and Table -- Acronyms and Abbreviations -- 1 Introduction and Overview -- 2 Developing First-in-Human Gene Therapy Clinical Trials -- 3 Understanding the Complexities of Patient Selection, Enrollment, and the Consent Process -- 4 Developing Endpoints for Gene Therapy Clinical Trials -- 5 Integrating Gene-Based Therapies into Clinical Practice: Exploring Long-Term Clinical Follow-Up of Patients -- 6 Reflections on the Workshop and Potential Opportunities for Next Steps -- References Appendix A: Workshop Agenda -- Appendix B: Speaker Biographical Sketches -- Appendix C: Statement of Task -- Appendix D: Registered Attendees |
| Physical Description: | 1 Online-Ressource ( 1 PDF file xx, 106 Seiten) illustrations |
| ISBN: | 9780309672993 0309672996 9780309673013 0309673011 |
Staff View
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| 245 | 1 | 0 | |a Exploring novel clinical trial designs for gene-based therapies |b proceedings of a workshop |c Siobhan Addie, Meredith Hackmann, Joe Alper, and Sarah H. Beachy, rapporteurs ; Forum on Regenerative Medicine, Board on Health Sciences Policy, Health and Medicine Division, the National Academies of Sciences, Engineering, Medicine |
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| 500 | |a Appendix A: Workshop Agenda -- Appendix B: Speaker Biographical Sketches -- Appendix C: Statement of Task -- Appendix D: Registered Attendees | ||
| 650 | 4 | |a Gene therapy | |
| 650 | 4 | |a Regenerative medicine |x Congresses | |
| 700 | 1 | |a Hackmann, Meredith |e Sonstige |4 oth | |
| 700 | 1 | |a Alper, Joe |e Sonstige |4 oth | |
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| spelling | Addie, Siobhan Verfasser aut Exploring novel clinical trial designs for gene-based therapies proceedings of a workshop Siobhan Addie, Meredith Hackmann, Joe Alper, and Sarah H. Beachy, rapporteurs ; Forum on Regenerative Medicine, Board on Health Sciences Policy, Health and Medicine Division, the National Academies of Sciences, Engineering, Medicine Washington, D.C. National Academies Press [2020] 1 Online-Ressource ( 1 PDF file xx, 106 Seiten) illustrations txt rdacontent c rdamedia cr rdacarrier Includes bibliographical references Intro -- FrontMatter -- Reviewers -- Acknowledgments -- Contents -- Boxes, Figures, and Table -- Acronyms and Abbreviations -- 1 Introduction and Overview -- 2 Developing First-in-Human Gene Therapy Clinical Trials -- 3 Understanding the Complexities of Patient Selection, Enrollment, and the Consent Process -- 4 Developing Endpoints for Gene Therapy Clinical Trials -- 5 Integrating Gene-Based Therapies into Clinical Practice: Exploring Long-Term Clinical Follow-Up of Patients -- 6 Reflections on the Workshop and Potential Opportunities for Next Steps -- References Appendix A: Workshop Agenda -- Appendix B: Speaker Biographical Sketches -- Appendix C: Statement of Task -- Appendix D: Registered Attendees Gene therapy Regenerative medicine Congresses Hackmann, Meredith Sonstige oth Alper, Joe Sonstige oth Beachy, Sarah H. Sonstige oth Erscheint auch als Druck-Ausgabe 9780309672986 Erscheint auch als Druck-Ausgabe 0309672988 https://search.ebscohost.com/login.aspx?direct=true&scope=site&db=nlebk&db=nlabk&AN=2591575 Verlag URL des Erstveröffentlichers Volltext |
| spellingShingle | Addie, Siobhan Exploring novel clinical trial designs for gene-based therapies proceedings of a workshop Gene therapy Regenerative medicine Congresses |
| title | Exploring novel clinical trial designs for gene-based therapies proceedings of a workshop |
| title_auth | Exploring novel clinical trial designs for gene-based therapies proceedings of a workshop |
| title_exact_search | Exploring novel clinical trial designs for gene-based therapies proceedings of a workshop |
| title_exact_search_txtP | Exploring novel clinical trial designs for gene-based therapies proceedings of a workshop |
| title_full | Exploring novel clinical trial designs for gene-based therapies proceedings of a workshop Siobhan Addie, Meredith Hackmann, Joe Alper, and Sarah H. Beachy, rapporteurs ; Forum on Regenerative Medicine, Board on Health Sciences Policy, Health and Medicine Division, the National Academies of Sciences, Engineering, Medicine |
| title_fullStr | Exploring novel clinical trial designs for gene-based therapies proceedings of a workshop Siobhan Addie, Meredith Hackmann, Joe Alper, and Sarah H. Beachy, rapporteurs ; Forum on Regenerative Medicine, Board on Health Sciences Policy, Health and Medicine Division, the National Academies of Sciences, Engineering, Medicine |
| title_full_unstemmed | Exploring novel clinical trial designs for gene-based therapies proceedings of a workshop Siobhan Addie, Meredith Hackmann, Joe Alper, and Sarah H. Beachy, rapporteurs ; Forum on Regenerative Medicine, Board on Health Sciences Policy, Health and Medicine Division, the National Academies of Sciences, Engineering, Medicine |
| title_short | Exploring novel clinical trial designs for gene-based therapies |
| title_sort | exploring novel clinical trial designs for gene based therapies proceedings of a workshop |
| title_sub | proceedings of a workshop |
| topic | Gene therapy Regenerative medicine Congresses |
| topic_facet | Gene therapy Regenerative medicine Congresses |
| url | https://search.ebscohost.com/login.aspx?direct=true&scope=site&db=nlebk&db=nlabk&AN=2591575 |
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